Juliette Hordeaux

I oversee translational research and discovery at Gemma biotherapeutics, a new company funded by Jim Wilson that aims to accelerate the development and global access of gene therapies for rare diseases. I am a DVM, board certified in Pathology (ECVP), and received my PhD from the University of Nantes where I specialized in in vivo gene therapy. I have worked in the translational AAV gene therapy field for 15 years. While at the Gene Therapy Program, I led a cross-functional team of scientists investigating AAV therapies for rare monogenic disorders, from POC to 5 successful IND filings. My special interests are AAV-mediated toxicity, investigative pathology, toxicity mechanism of actions, and ways to develop safer gene therapy modalities.